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CPC-086 Miglustat Off-Label in a Paediatric Formulation For a Rare Metabolic Disease: Early Infantile GM1 Gangliosidosis
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Garzone A, Pompilio A, Ciuccarelli F, et al
CPC-086 Miglustat Off-Label in a Paediatric Formulation For a Rare Metabolic Disease: Early Infantile GM1 Gangliosidosis