Niemann Pick disease type C

Intrathecal cyclodextrin in the treatment of Niemann-Pick disease type C
Maria Roch Santed, Maria Josep Cabañas Poy, Mireia Del Toro Riera, Carme Cañete Ramírez, Aurora Fernández Polo, Susana Clemente Bautista

European Journal of Hospital Pharmacy May 2017, 24 (3) 185-188; DOI: 10.1136/ejhpharm-2016-001067

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Niemann Pick disease type C